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Sarepta, gene therapy

Patient dies in Sarepta gene therapy trial, adding to safety concerns

The death will likely further stoke safety concerns around Sarepta's gene therapies, as well as raise questions around the company’s transparency.

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· 1h · on MSN

Sarepta Falls After Another Patient Dies on Gene Therapy

BioPharma Dive · 45m

Patient reportedly dies in Sarepta study of limb-girdle gene therapy

Neurology Advisor1h

Child’s Rare Neurodegenerative Disease Fuels Therapy Innovation: Paxton’s Story

The Purdy family shares their insights on navigating their child’s rare neurodegenerative disease and their direct ...

Miltenyi Biotec and THSTI FIVE partner to launch India’s first hands-on CAR-T cell and gene therapy training curriculum

Our Bureau, Mumbai Friday, July 18, 2025, 17:45 Hrs [IST] ...

Fierce Healthcare2d

CMS officially names participants in Cell and Gene Therapy Access Model

The Centers for Medicare and Medicaid Services (CMS) has selected 35 participants for its new, voluntary Cell and Gene ...

InvestorsHub on MSN1d

Rocket Pharmaceuticals Shares Jump After FDA Grants Accelerated Review Status to Gene Therapy

Rocket Pharmaceuticals Inc. (NASDAQ:RCKT) surged 15% after receiving a key regulatory boost from the U.S. Food and Drug ...

Sarepta Tags DMD Gene Therapy Elevidys With Black Box Warning, Axes 500 Staff

Following the death of two teenage patients with Duchenne muscular dystrophy following Elevidys treatment, Sarepta ...

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