Cerebral adrenoleukodystrophy (CALD) is a rare progressive, genetic brain disease that primarily presents in young boys, ...

LONDON and NEW YORK, Oct. 09, 2024 (GLOBE NEWSWIRE) -- MeiraGTx Holdings plc (Nasdaq: MGTX), a vertically integrated, clinical stage genetic medicine company, today announced a poster presentation at ...

Wendy Fry had just celebrated her first Christmas with her first child, 8-month-old Penny, when she woke the next day to another first: Her daughter having her first seizure. "I have never felt ...

You feel you could benefit from therapy, but you know upfront that you can’t do any long-term treatment—your insurance won’t ...

Medical experts and patients have alerted the Nigerian public to the many challenges faced by people with tuberculosis (TB) ...

Fratricide-resistant CD7 CAR-T therapy by NUS proves effective in treating relapsed or refractory T-cell leukaemia SINGAPORE, ...

Mattel is celebrating the launch of its new Barbie by partnering with the University of Michigan's C.S. Mott Children's ...

Approximately 3.3 million children in the United States are taking medication for ADHD. Yet only 33% are receiving a ...

Evidence is rising in favor of using highly effective DMTs to treat pediatric MS, but with few licensed for pediatric use, it ...

By September, at least 30 people worldwide had begun a one-time gene therapy ... child. Both Vertex and Bluebird have ...