News

At the FDA's request, delandistrogene moxeparvovec (Elevidys), the only approved gene therapy for Duchenne muscular dystrophy ...
Sarepta Therapeutics Inc. said another patient has died from acute liver failure after receiving one of its gene therapies, ...
A 51-year-old man died last month after receiving an experimental treatment from Sarepta, the third death this year tied to ...
Tiny fat bubbles carrying gene therapy have successfully repaired DNA in the lungs and liver of animals with alpha-1 ...
The family, Syrian nationals residing in the UAE, had launched an emotional plea on social media to save their daughter who ...
Sarepta Therapeutics (SRPT) said a third patient has died from acute liver failure after receiving one of its gene therapies, intensifying scrutiny over the safety of its treatments, Bloomberg ...
AAVB-039 advances gene therapy for Stargardt disease, aiming for innovative treatments for inherited retinal disorders.
Sarepta Therapeutics appears to have right-sized itself after laying off over a third of its staff, announcing a significant ...
Discover the current pipeline candidates advancing through the clinic for the treatment of sickle cell disease.
The US Food and Drug Administration (FDA) recently granted fast track designation to Sanofi’s SAR446597 for the treatment of geographic atrophy (GA). 1 ...
Sarepta Therapeutics, Inc. faces setbacks with Elevidys, safety issues, and workforce cuts, raising concerns about its ...